Muscular Dystrophy Association Marks Rare Disease Day by Spotlighting Community Stories Driving Progress in Research, Care, ...
Sarepta’s blockbuster gene therapy has come under scrutiny following a string of patient deaths.
By Mariam Sunny Jan 26 (Reuters) - Sarepta Therapeutics' gene therapy for Duchenne muscular dystrophy slowed disease ...
In his CEO Commentary, Frederic Revah, Ph.D., underscores the dedication, expertise and successes of Genethon's 240 scientists and professional staff as they pursue new gene therapy treatments for ...
Manistee News Advocate on MSN
AMISH KITCHEN: Daughter Verena discusses her disability
"Muscular dystrophy can take many things from me, but it will not take away my happiness, nor will it take away my faith." ...
This quick alphabetical guide will help you feel more confident when talking about muscular dystrophy with your doctor and loved ones. Muscular dystrophy is the name for a group of genetic diseases ...
Disability advocate TaLisha Gryzb is a mother of four living with muscular dystrophy who educates viewers about her ...
Researchers from Carnegie Mellon University have discovered a way to target RNA that could lead to new treatment options for ...
In research published in Developmental Medicine & Child Neurology, investigators have developed a brief, reliable, and valid ...
Zeleciment basivarsen (z-basivarsen) demonstrated sustained functional improvement across multiple clinical measures in the ongoing ACHIEVE ...
Jan 26 (Reuters) - Sarepta Therapeutics' gene therapy for a progressive muscle‑wasting disorder showed sustained benefit in ...
Muscular dystrophy is a group of disorders that involve a progressive loss of muscle mass and consequent loss of strength. In general, the condition is caused by genetic variations that interfere with ...
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