JABSOM Cell and Molecular Biology researcher Dr. Jesse Owens has spent the better part of two decades chasing a vision that ...

Researchers at the Children's Hospital of Philadelphia are responsible for helping develop a new gene therapy treatment for ...

A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a ...

Findings from two clinical trials suggest Novartis' Itvisma is safe and effective for SMA patients over two years old.

Backed by a handful of prominent investors including the Gates Foundation, the startup is pursuing an approach it believes ...

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University's College ...

A cutting-edge base-edited CAR T-cell therapy is opening a revolutionary new frontier for patients battling aggressive T-cell ...

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University’s College ...

Scientists at UCL and GOSH have used groundbreaking base-edited CAR‑T cell therapy — BE‑CAR7 — to treat aggressive T‑cell ...

The treatment uses a modified, harmless virus to deliver healthy genes to a patient’s cells to treat genetic diseases. Read ...

T therapy has helped previously untreatable for T-cell acute lymphoblastic leukemia patients achieve remission, with 82% ...

Menopausal hormone therapy (MHT) does not raise breast cancer risk in women with breast cancer gene mutations, while estrogen only MHT leads to reduced risk.