Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE) is one of the Best 52-Week Low Stocks to Buy According to Analysts.

It is trying to treat a devastating lifelong disease by fixing it at its source. We are able to fix the actual genetic ...

A discovery with major implications for cancer treatment has been made by a team of researchers from Rensselaer Polytechnic ...

"We want to begin to address these challenges therapeutically." NF1 is caused by mutations in a gene that produces neurofibromin, a protein that plays a key role in regulating cell growth and ...

Fragile X disorders include two distinct conditions: fragile X syndrome (the most common single-gene cause of developmental delay and autism) and an entirely separate group of premutation syndromes.